Enduring Future Direction of Lab Medicine: Sickle cell disease: How new technologies are transforming patient lives

Course overview

In this "Future Direction of Laboratory Medicine" webinar, Maggie DiGuardo, M.D. and Justin Juskewitch, M.D., Ph.D., will review the current knowledge regarding sickle cell disease from its genetic cause to the myriads of effects in can have for affected individuals. Through the lens of a clinical case study, they will describe the current treatment modalities available for long-term management of patients with sickle cell disease. The presenters will then explore the new gene therapy-based treatments for sickle cell disease and the clinical trials that supported the recent FDA approval. Learning Objectives: 1. Describe the prevalence and pathophysiology of sickle cell disease. 2. Summarize current clinical management approaches with associated challenges and limitations. 3. State new treatment modalities and potential patient impact.