CRISPR TECHNOLOY SIMPLY EXPLAINED AND NEUROLOGICAL DISORDERS

Course overview

CRISPR is a groundbreaking gene editing technology that allows scientists to precisely cut and modify DNA within living organisms. Adapted from a natural defense system found in bacteria, CRISPR uses a specialized protein Cas9 guided by RNA to target specific genetic sequences. This makes it possible to correct mutations, study gene functions, and explore potential treatments for a wide range of diseases with unprecedented accuracy and efficiency. Neurological disorders such as Parkinsons disease, Alzheimers disease, Huntingtons disease, and ALS have long been managed with symptomatic treatments that rarely address their root causes. Recent advances in CRISPR gene-editing technology are changing that paradigm, opening the door to targeted therapies that can repair or silence faulty genes at their source. This course explores the science of CRISPR and its application in neurology, including delivery challenges to the brain and spinal cord, current research breakthroughs, clinical trial data, and the ethical considerations of editing the human genome. Participants will gain a strong foundation in how CRISPR works, the potential benefits and risks of its use in neurological medicine, and the future landscape of gene based therapies